A 6-year-old girl with a rare inherited blindness regained vision through gene therapy, helping her see in low light again.

Epilepsy affects more than 50 million people worldwide, making it one of the most common neurological disorders. Although ...

The development of a pioneering gene therapy to treat a devastating, rare immune disorder led by UCL scientists is set to ...

Scientists from the Centenary Institute and the University of Sydney have made a landmark discovery that could lead to safer and more effective gene therapies for a range of serious genetic disorders ...

An eight-month-old infant with rare but severe epilepsy has received an experimental gene replacement in a historic medical moment. The child was one of the first in the world to be treated with gene ...

Genespire , in collaboration with researchers at the San Raffaele Telethon Institute for Gene Therapy (SR-TIGET) , has today announced the ...

As other gene editing programs fold or get sold, Arbor Biotechnologies has secured $73.9 million to advance its lead liver-targeting gene therapy into human trials. The series C was led by Arch ...

The idea behind intra-articular gene therapy for treating osteoarthritis (OA) is to deliver the gene-altering vector or cells directly to the precise site of the disease with a single injection — so ...

A gene therapy that instructs cells to produce more of an anti-ageing protein called klotho is about to be offered by a US company at overseas clinics to bypass FDA rules ...